Oct. 24, 2023 One problem in gene therapy is that not all genes transfer equally well into the target cells. Researchers have now developed a flexible method to transfer large genes efficiently and without ...
Aug. 30, 2023 A clinical trial has tested a potentially curative stem cell gene therapy for sickle cell disease. The results were ...
Aug. 11, 2023 Researchers have developed a new form of gene therapy that can stop cell division in fusion-driven ...
Aug. 10, 2023 A change in just one letter in the code that makes up a cancer-causing gene can significantly affect how aggressive a tumor is or how well a patient with cancer responds to a particular therapy. A ...
Aug. 10, 2023 Researchers have made a remarkable step forward in finding a potential cure for a type of childhood kidney ...
Aug. 10, 2023 New research has successfully reversed hearing loss in mice. Scientists used a genetic approach to fix deafness in mice, restoring their hearing abilities in low and middle frequency ...
Aug. 9, 2023 A study shows new steps toward more patients getting gene ...
July 27, 2023 In a step forward in the development of genetic medicines, researchers have developed a proof-of-concept model for delivering gene editing tools to treat blood disorders, allowing for the ...
July 12, 2023 Cancer therapies that target specific genetic abnormalities in tumors have revolutionized treatment possibilities over the past two decades. While quality of life and survival are improved with ...
May 30, 2023 A scientific team has designed a strategy to fight obesity and diabetes in mice through ex vivo gene therapy which consists of implanting cells that have been manipulated and transformed in order to ...
Apr. 4, 2023 Researchers uncover a mechanism in a retinal transporter protein that causes blindness, could lead to targeted ...
Feb. 17, 2023 Researchers used the drug fasudil to restore neurons and improve methamphetamine-induced cognitive dysfunction in a mouse model of ...
Jan. 24, 2023 Researchers have uncovered a gene that is overexpressed in mutated IDH1. Studies in human cells and a novel mouse model both show that this gene, called ZMYND8, plays a critical role in the radiation ...
Jan. 11, 2023 Scientists have demonstrated in animal models the possibility of using lipid nanoparticles and messenger RNA, the technology underpinning COVID-19 vaccines, to treat blindness associated with a rare ...
Dec. 7, 2022 Research has found that misfolded proteins in liver cells contribute to the development of liver cancer, shedding new light on the mysterious origins of one of the world's deadliest diseases. ...
Nov. 9, 2022 Technology that can change skin tissue into blood vessels and nerve cells also shows promise as a treatment for traumatic muscle ...
Nov. 3, 2022 A new treatment for neurological and psychiatric diseases, that works by reducing the excitability of overactive brain cells, has been ...
Oct. 26, 2022 A fault in cells that form a key part of the immune system can be repaired with a pioneering gene editing technique, finds new research demonstrated in human cells and ...
Oct. 20, 2022 A new study identifies common and rare gene mutations that impact radiation resistance and sensitivity, an important step toward providing more individualized and effective radiotherapy for patients ...
Oct. 19, 2022 Research led by doctors and scientists have identified a gene that may provide a therapeutic target for the deadly, treatment-resistant brain cancer glioblastoma multiforme ...